- Dokumeninformediunggah olehalvaro.bosch.ibanez
- Dokumenjamaneurology_mendell_2021_oi_210023_1624467431.00495diunggah olehalvaro.bosch.ibanez
- Dokumeninforme (1)diunggah olehalvaro.bosch.ibanez
- Dokumeninforme (2)diunggah olehalvaro.bosch.ibanez
- DokumenAtrofia_muscular_espinaldiunggah olehalvaro.bosch.ibanez
- DokumenGil Lizarraga, Uxuediunggah olehalvaro.bosch.ibanez
- DokumenSpinal Muscular Atrophydiunggah olehalvaro.bosch.ibanez
- DokumenSpinal muscular atrophy From approved therapies to future therapeutic targets for personalized medicinediunggah olehalvaro.bosch.ibanez
- DokumenSafety and efficacy of nusinersen in spinal muscular atrophy The EMBRACE studydiunggah olehalvaro.bosch.ibanez
- DokumenNew and Developing Therapies in Spinal Musculardiunggah olehalvaro.bosch.ibanez
- DokumenExpert recommendations and clinical considerations in the use of onasemnogene abeparvovec gene therapy for spinal muscular atrophydiunggah olehalvaro.bosch.ibanez
- DokumenAdvances and limitations for the treatment of spinal muscular atrophydiunggah olehalvaro.bosch.ibanez
- DokumenFive-Year Extension Results of the Phase 1 START Trialdiunggah olehalvaro.bosch.ibanez